Results
Research > Drug Development
Should Your Child Participate in a Clinical Trial? A Parent's Decision Framework
How to evaluate trial participation: phase, risk categories, volunteer rights, investigator credibility, and peer support networks.
Research > Drug Development
Fragile X Drug Trials: The First Real Breakthroughs and What They Mean for Families
After years of failed trials, Zatolmilast and SPG601 represent real progress for Fragile X treatment. What families need to know.
Research > Drug Development
The Drug Development Pipeline for Special Needs: What Parents Need to Know About How Treatments Go from Lab to FDA Approval
The 12-15 year drug approval timeline from preclinical research to FDA review, explained for families navigating treatment options.
Research > Drug Development
Unveiling Breakthroughs in Muscular Dystrophy Treatment
Muscular dystrophy research advances gene therapy, inflammation control, and assistive devices, empowering patients and offering hope.
Research > Drug Development
Turning Basic Research into Better Treatments
The Myelin Repair Foundation aims to accelerate myelin repair therapy for MS and revolutionize medical research with its ARC Model.
Research > Drug Development
Muscular Dystrophy Drug Success
Ohio State Univ. researchers find drugs lisinopril and spironolactone help preserve muscle in DMD, potentially extending lives.